| The Impact of Dupilumab Treatment on Anxiety and Depression Symptoms in Patients with Moderate-to-Severe Atopic Dermatitis in Gulf Countries: DERMIND-AD |
Ongoing |
Dupilumab |
4 |
OBS18647 |
1.King Faisal Specialist Hospital and Researech Center - Jeddah 2. National Guard Hospital - Riyadh 3.King Abdulaziz University Hospital - Jeddah |
| REal-World Application of Luspatercept in Adults with Transfusion-Dependent beta-Thalassemia in the Middle East (RELATE): A non-interventional retrospective and prospective observational study |
Ongoing |
luspatercept |
4 |
CA056-1107 |
1. Prince mohammed bin fahad hosputal - Qatif 2. King Saud University Medical city - Riyadh 3. Alnoor specialist hospital - Madinah 4. Hereditary Blood Disease Center - Alahsa |
| 3-Arm Study to Investigate the Safety and Efficacy of Efimosfermin Alfa in Participants With Biopsy-Confirmed F2- or F3-Stage Metabolic Dysfunction-Associated |
Ongoing |
Efimosfermin alfa |
3 |
301160 |
1.King Fahad Specialist Hospital - Dammam 2.King Abdulaziz Medical City - Jeddah 3.Imam Abdulrahman Bin Faisal University - Dammam |
| A Phase 3, Randomized, Double-Blind, Placebo-Controlled, 3-Arm Study to Investigate the Safety and Tolerability of Efimosfermin Alfa in Participants With Known or Suspected F2- or F3-Stage Metabolic Dysfunction-Associated Steatohepatitis (MASH) (ZENITH-2) |
Ongoing |
Efimosfermin alfa |
3 |
306246 |
1.King Fahad Specialist Hospital - Dammam 2.King Faisal Specialist Hospital and Researech Center - Riyadh 3.King Abdulaziz Medical City - Jeddah 4.Imam Abdulrahman Bin Faisal University - Dammam |
| A Randomized, Double-Blind, Multicenter, Placebo-Controlled Study to Evaluate the Safety and Efficacy of Atumelnant in Adult Participants with Classic Congenital Adrenal Hyperplasia |
Ongoing |
atumelnant/ CRN04894 |
3 |
CRN04894-12 |
1. King Faisal Specialist Hospital and Researech Center - Riyadh 2. National Guard Health Affairs - Riyadh 3.King Saud University Medical City - Riyadh 4.King Fahad Specialist Hospital - Dammam 5. King Abdullah International Medical research Center - Jeddah |
| A Multi-Center, Non-Interventional Study on Effectiveness and Treatment Persistence of Guselkumab in Patients with ULcerative Colitis and Crohn’s DiseasE in Real-World Practice in Saudi Arabia (EAGLE) |
Ongoing |
Tremfya (Guselkumab) |
4 |
CNTO1959IB |
1. King Abdullah Medical City - Makkah 2. Integrated gut center - Jeddah |
| A phase 3, multicenter, randomized, double-blind, placebo-controlled, parallel-group study with an open-label period and long-term extension to assess the efficacy and safety of rilzabrutinib in participants with warm autoimmune hemolytic anemia (wAIHA) |
Ongoing |
Rilzabrutinib SAR444671 |
3 |
EFC17360 |
1.King Saud University Medical City -Riyadh 2.King Faisal Specialist Hospital and Researech Center - Jeddah |
| A Phase 2/3 Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of Atumelnant Treatment in Pediatric Participants with Congenital Adrenal Hyperplasia Including a Long-Term Extension |
Ongoing |
atumelnant/ CRN04894 |
2/3 |
CRN04894-13 |
1.King Saud University Medical City -Riyadh 2. King Faisal Specialist Hospital and Research Center - Riyadh |
| Subcutaneous Fast Acting Insulin Versus Intravenous Regular Insulin Infusion in The Management of Moderate and Severe Diabetic Ketoacidosis Among Children with Type I Diabetes Mellitus: A Pilot Randomized Open Label-Controlled Trial |
Ongoing |
Insulin Aspart |
3 |
E-25-9801 |
1.King Saud University Medical City -Riyadh |
| A Phase 3,2-Part,Randomized,Double-Blind,Placebo-Controlled Study(Part 1)and Open-Label Extension(Part 2)to Evaluate the Efficacy,Safety,Pharmacokinetics,and Pharmacodynamics of Omaveloxolone(BIIB141)in Participants With Friedreich’s Ataxia Aged 2 to < 16 |
Ongoing |
Omaveloxolone (BIIB141) |
3 |
296FA301 |
1.King Faisal Specialist Hospital and Researech Center - Riyadh |
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